![Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society](https://www.oligotherapeutics.org/wp-content/uploads/2021/01/Pre-mRNA-1ysv-tubes-cc-500x383.png)
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society
![Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society](https://www.oligotherapeutics.org/wp-content/uploads/2018/03/Nusinersen-III.png)
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society
Therapeutic decisions under uncertainty for spinal muscular atrophy: The DECISIONS-SMA study protocol | PLOS ONE
![Discovery of a Small Molecule Probe That Post-Translationally Stabilizes the Survival Motor Neuron Protein for the Treatment of Spinal Muscular Atrophy | Journal of Medicinal Chemistry Discovery of a Small Molecule Probe That Post-Translationally Stabilizes the Survival Motor Neuron Protein for the Treatment of Spinal Muscular Atrophy | Journal of Medicinal Chemistry](https://pubs.acs.org/cms/10.1021/acs.jmedchem.6b01885/asset/images/medium/jm-2016-018859_0013.gif)
Discovery of a Small Molecule Probe That Post-Translationally Stabilizes the Survival Motor Neuron Protein for the Treatment of Spinal Muscular Atrophy | Journal of Medicinal Chemistry
![Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy - Oligonucleotide Therapeutics Society](https://www.oligotherapeutics.org/wp-content/uploads/2021/08/Nusinersen-II-300x300-1.png)