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Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study - The Lancet Neurology
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![NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC](https://pbs.twimg.com/media/Dpo0LXuU8AARxgn.jpg)
NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC
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